experimental drugs

Federal law requires publicly funded medical researchers to promptly report the results of many experimental treatments. But few are doing so, a review shows, and patients may be hurt.

When a child falls ill with cancer, many of the drugs that might help are either experimental or unapproved for use in kids.

There is no effective treatment for the rare genetic disorder fragile X syndrome, so two parents created a foundation to fund research. But they found there's no easy road to a cure.

While several states have approved so-called right-to-try measures that aim to give patients with life-threatening illnesses access to unapproved drugs, drugmakers don't have to comply.

Future outbreaks of superbugs that resist treatment will test the American health care system's ability to respond. A prominent patient advocate says we need to be ready.